Anything for a Cure—People Magazine

Mar 21, 2005 | EDITORIALS

By: By Richard Jerome. Macon Morehouse in San Antonio. posted on: March 21, 2005 Doctors Said Tiffany House Wouldn’t Live Past 20, but Her Parents Refused to Accept That Death Sentence (Published in People Magazine: March 21, 2005) When Randall and Marylyn House...

Summary of 2004 International Pompe Association Conference

Oct 12, 2004 | NEWS

On 9th and 10th October, the AGSD (UK) held its annual patient conference. This year we were more ambitious than usual in that the Pompe Workshop extended into a second day. Families and speakers arrived on the Friday night and we held an informal conference dinner on...

IPA Conference – October 30 – November 1, 2003

Nov 3, 2003 | NEWS

Medical experts and patients are invited to attend the International Pompe Conference 2003. The goal of the conference is to bring together scientific expertise and patients’ experience. On the way towards a therapy for Pompe’s Disease there were and are many examples...

Genzyme Begins Enrolling Patients in Pivotal Pompe Disease Study

May 29, 2003 | NEWS

Genzyme General (Nasdaq: GENZ), a division of Genzyme Corp., announced today that it has treated the first patient in a pivotal clinical trial evaluating the use of its MyozymeTM recombinant human acid alpha-glucosidase enzyme (rhGAA) as a potential treatment for...

Editorial: Response to March 2003 Article in Quest

Mar 28, 2003 | EDITORIALS

By: Marylyn House posted on: March 28, 2003 The following correspondence is in response to the Pompe disease research article that was published in the March 2003 issue of “Quest” an MDA publication. It includes emails sent over the GSDnet during February-March 2003,...

Genzyme General Begins Enrolling Patients in Pompe Disease Study

Mar 20, 2003 | NEWS

CAMBRIDGE, Mass – Genzyme General (Nasdaq: GENZ), a division of Genzyme Corp., announced today that it has begun enrolment in a clinical trial evaluating the use of its Myozyme™  recombinant human acid alpha -Glucosidase enzyme as a potential treatment for Pompe...

Genzyme’s Pompe Program Update

Dec 2, 2002 | NEWS

An update by Genzyme regarding treatment for Pompe disease. Q: What is the status of the Pompe program? Genzyme has made strong progress within its Pompe disease program since its decision earlier this year to move forward with an internally developed product...

IPA/Genzyme News—September 24, 2002

Oct 2, 2002 | NEWS

IBaarn, October 2nd 2002 Dear IPA members, Herewith I would like to inform you about the IPA/Genzyme telephone conference of September 24 2002. We discussed issues concerning the production, the transition, new trials and the meeting with the Erasmus University, VSN,...