May 11th 2005 IPA Conference Pompe’s disease Nantes, France.
“Emerging therapies for Pompe disease”
Dr. Ans van der Ploeg, Erasmus MC Rotterdam the Netherlands, talked about the natural course in late onset Pompe disease. She informed the audience about the outcome and the importance of the IPA Erasmus MC Patient survey (questionnaire). For information about the outcome of the survey we would like to refer to the publications mentioned below.
View complete summary here.