An Open Letter to the Pompe Community

November 1, 2022

On October 28, Amicus Therapeutics issued a press release with an update on the progress of our Pompe
program as we received information from the US Food & Drug Administration (FDA) on the regulatory status of
our next-generation therapy for the treatment of late-onset Pompe disease. The entire Pompe community –
from individuals and families to patient advocacy organizations and their leaders – are our valued partners and
we want to share this information with you all within the context of the regulatory activities’ timeline.

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OTHER NEWS

An Open Letter to the Pompe Community

On October 28, Amicus Therapeutics issued a press release with an update on the progress of our Pompe program as we received information from the US Food & Drug Administration (FDA) on the regulatory status of our next-generation therapy for the treatment of...

read more

International Survey on Pompe Disease and Covid-19

Over the last 2 years the COVID-19 pandemic has had wide reaching effects on people all over the world. To better understand the impact of the Covid 19 Pandemic on the worldwide Pompe community, the International Pompe Association and the Erasmus MC are undertaking a...

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2022 PCMA Pull for Pompe Fundraiser

The AMDA is excited to announce that the 11th Annual PCMA’s Pull for Pompe will take place on Saturday, April 30, 2022 at the National Shooting Complex in San Antonio, Texas! The Pull for Pompe clay shooting event is designed for all ages and ability levels. Please...

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 Acid Maltase Deficiency Association

GET INVOLVED

Your generous contribution will go a long way into improving the quality of life of Pompe Disease Patients worldwide. Donations go towards Pompe Disease Research.

If you are interested in learning more about Pompe Disease and would like to make a contribution in support of necessary research, please contact us at:

(210) 494-6144

info@amda-pompe.org

AMDA

PO Box 700248

San Antonio, Texas 78270 USA