A Heartfelt Thank You to the Krueger Family The Acid Maltase Deficiency Association is deeply grateful to the Krueger family

Webinar Details Title: Mental Health for Pompe DiseaseA rare genetic disease in which the body cannot properly break down glycogen, leading to buildup that damages muscles and can affect breathing and, in some cases, the heart.: The Importance of Being Understood Date: Thursday, May 14, 2026 Speakers:Heather ShortenNadia Bodkin,

Webinar Details Title: Immune ResponsesThe body's natural defense system reacting to substances it sees as foreign, including treatments like enzyme replacement therapy or gene therapy. to AAVA harmless virus commonly used as a delivery system in gene therapy to carry healthy genes into cells. Gene TherapyA developing treatment that aims to fix, replace, or add genetic instructions.: Challenges and Emerging Solutions Date: Thursday, April 23, 2026 Speaker:Abigail Benkert, MD

We are honored to share this moment recognizing Tiffany House as a recipient of the RareVoice Award for State Advocacy.

The AMDA is excited to announce that the 15th Annual PCMA’s Pull for Pompe fundraiser will take place on Saturday,

Webinar Details Title: Making sense of research studies and registries Date: Thursday, February 19, 2026 Speakers:Karmen TrzupekRyan Colburn Webinar Overview:Have you

The Acid Maltase Deficiency Association (AMDA) is deeply grateful to the individuals, families, and organizations who contributed in 2025. Your

Webinar Details Title: Grief Happens in Rare Disease: Let’s Talk About it Already Date: Thursday, January 15, 2026 Speaker:Lisa Keefauver,

At Sanofi’s inaugural Global Rare Impact Awards ceremony held on November 14, 2025, in Vienna, three extraordinary leaders were recognized