June 1, 1998
Gene Therapy: National Institutes of Health
National Institutes of Health Paul Plotz, M.D., Nina Raben, M.D., Ph.D. Nina Raben, M.D., Ph.D., NIH Research Chemist, visited the
Human Molecular Genetics, January 1998 “Generalized glycogenA stored form of sugar used for energy. More storage and cardiomegaly in a knockout mouse modelA laboratory mouse used to study disease and test treatments before human trials. More of Pompe diseaseA rare genetic disease in which the body cannot properly break down glycogen, leading to buildup tha... More” by A.
November 30, 1996
Gene Therapy: Johns Hopkins University
Johns Hopkins University Barry J. Byrne, M.D., Ph.D. Paul D. Kessler, M.D. The following is a summary of the publication
October 30, 1996
