Second Annual International Pompe Day!

Feb 1, 2015 | NEWS

April 15th, 2015 will mark the Second Annual International Pompe Day! Last year the Pompe Community worked together to raise awareness of Pompe Disease, and showed the world how Strong our Community can be. Please click here for a summary of the events and activities...

Update on Biomarin’s Pompe Clinical Program—January 2015

Jan 6, 2015 | NEWS

BioMarin are pausing further recruitment for their BMN-701 clinical trial and have provided this programme update: January 2015 BioMarin is pleased to update the Pompe patient community on the progress made in our programme to develop a treatment for people living...

2014 Helen Walker Research Grant Awarded

Dec 15, 2014 | NEWS

The fifth annual AMDA Research Grant (the 2014 Helen Walker Research Grant) was awarded to Dr. Giancarlo Parenti with the Federico II University in Naples, Italy for his Project: “Analysis of Circulating and Tissue Specific microRNAsSmall molecules that help control...
Design And Performance Of Clinical Trials: An Overview

Design And Performance Of Clinical Trials: An Overview

Oct 20, 2014 | PAST WEBINARS

Webinar Details Title: Design and Performance of Clinical Trials: An Overview Date: Monday, October 20, 2014 Speaker:Anne Zajicek, MD, PharmD, FAAP, Chief, Obstetric and Pediatric, Pharmacology and Therapeutics Branch, National Institute of Child Health and Human...

United States Pompe Community Update from Genzyme

Oct 17, 2014 | NEWS

Genzyme would like to share with you an important update regarding the recent United States (U.S.) Food and Drug Administration’s (FDA) approval of an expanded label for Lumizyme® (alglucosidase alfa) manufactured at the 4000L scale and its impact on Myozyme®...

2014 Helen Walker Research Grant Now Accepting Applications

Jul 13, 2014 | NEWS

The AMDA is excited to announce a research grant opportunity for applicants who are involved in Pompe Disease research. This grant opportunity was made possible by a fundraiser hosted by the Precast Manufacturer’s Association of Texas (PCMA of Texas) on April 5,...

AMDA to Celebrate First International Pompe Day!!

May 4, 2014 | NEWS

Update: May 4, 2014 THE AMDA TO CELEBRATE THE FIRST INTERNATIONAL POMPE DAY WITH COMMEMORATIVE BOOK April 15, 2014 marked the International Pompe Association’s (IPA) first annual International Pompe Day.  In honor of the First International Pompe Day, the Acid Maltase...