European Commission Approves Genzyme’s Myozyme®

Apr 4, 2006 | NEWS

Product is First Treatment for Pompe DiseaseA rare genetic disease in which the body cannot properly break down glycogen, leading to buildup tha... More Genzyme Corp. (Nasdaq: GENZ) announced today that it has received marketing authorization for Myozyme®...

Genzyme Provides Update on U.S. Marketing Application for Myozyme

Jan 18, 2006 | NEWS

Genzyme Corp. (Nasdaq: GENZ) announced today that the Food and Drug Administration has extended by 90 days the review period for the biologics license application for Myozyme® (alglucosidase alfaA form of enzyme replacement therapy used to treat Pompe disease by...

The IPA Pompe Connections Brochure

Oct 2, 2005 | NEWS

The IPA has developed the Pompe connections brochure to help get patients and their families timely and relevant information about Pompe diseaseA rare genetic disease in which the body cannot properly break down glycogen, leading to buildup tha... More and the...

Genzyme Submits BLA for Myozyme® for Treatment of Pompe Disease

Jul 30, 2005 | NEWS

Genzyme Corp. (Nasdaq: GENZ) announced today that it has submitted a biologics license application (BLA) to the U.S. Food and Drug Administration for Myozyme® (alglucosidase alfaA form of enzyme replacement therapy used to treat Pompe disease by providing a lab-made...

Summary of the 2005 AFM-IPA Conference

May 13, 2005 | NEWS

May 11th 2005 IPA Conference Pompe’s disease Nantes, France. “Emerging therapies for Pompe diseaseA rare genetic disease in which the body cannot properly break down glycogen, leading to buildup tha... More” Dr. Ans van der Ploeg, Erasmus MC Rotterdam the Netherlands,...

Genzyme Reports Interim Results from Pivotal Study of Myozyme

Apr 26, 2005 | NEWS

CAMBRIDGE, Mass.—Genzyme Corp. (Nasdaq: GENZ) announced today that it has completed a planned analysis of interim data from its pivotal clinical trialA research study that tests new treatments or approaches in people. More of Myozyme® (alglucosidase alfaA form of...

Anything for a Cure—People Magazine

Mar 21, 2005 | EDITORIALS

By: By Richard Jerome. Macon Morehouse in San Antonio. posted on: March 21, 2005 Doctors Said Tiffany House Wouldn’t Live Past 20, but Her Parents Refused to Accept That Death Sentence (Published in People Magazine: March 21, 2005) When Randall and Marylyn House...

Summary of 2004 International Pompe Association Conference

Oct 12, 2004 | NEWS

On 9th and 10th October, the AGSD (UK) held its annual patient conference. This year we were more ambitious than usual in that the Pompe Workshop extended into a second day. Families and speakers arrived on the Friday night and we held an informal conference dinner on...