Spark Therapeutics Gene Therapy Research Webinar

Spark Therapeutics Gene Therapy Research Webinar

Sep 25, 2018 | PAST WEBINARS

Webinar Details Title: Spark Therapeutics Gene Therapy Research Webinar Date: Tuesday, September 25, 2018 Speakers:Federico Mingozzi, PhD – Chief Scientific OfficerPaul Monahan, MD – Translation Medicine Leader, Metabolic DisordersAmy Fisher, MS, CGC...

AMDA Webinar: Spark Therapeutics Gene Therapy Research

Sep 16, 2018 | NEWS

SPARK THERAPEUTICS GENE THERAPY RESEARCH WEBINAR Please join the AMDA for a webinar focused on Spark Therapeutics and gene therapyA developing treatment that aims to fix, replace, or add genetic instructions. More research Take this opportunity to learn more about...

Press Release from Erasmus Medical Center: Making Muscle from Skin

Jun 26, 2018 | NEWS

Researchers from the Erasmus MC in Rotterdam, Netherlands, have succeeded in generating muscle cells from skin cells. This is significant as skin cells can be relatively easily obtained from a skin biopsy. The team developed a protocol to obtain pure muscle cells (ie...

Valerion Initiates VAL-1221 Dosing in Patients with Pompe Disease

Jul 11, 2017 | NEWS

CONCORD, Mass., July 11, 2017—Valerion Therapeutics, a clinical-stage biotechnology company that specializes in the development of therapies for orphan genetic diseases, today announced that it has initiated dosing in a Phase 1/2 clinical trialA research study that...