Definition:
Short pieces of genetic material designed to change how a gene is read, potentially correcting faulty instructions.
Related Terms:
gene therapy, splicing (gene splicing), GAA gene, glycogen synthase (GYS 1)
News Archives
- April 2026 (13)
- March 2026 (6)
- February 2026 (3)
- January 2026 (4)
- December 2025 (2)
- November 2025 (2)
- October 2025 (4)
- September 2025 (2)
- August 2025 (2)
- July 2025 (3)
- June 2025 (3)
- April 2025 (1)
- March 2025 (3)
- February 2025 (2)
- January 2025 (4)
- December 2024 (12)
- November 2024 (2)
- October 2024 (1)
- September 2024 (1)
- August 2024 (3)
- June 2024 (1)
- May 2024 (1)
- February 2024 (2)
- January 2024 (1)
- December 2023 (2)
- November 2023 (1)
- October 2023 (3)
- September 2023 (1)
- August 2023 (4)
- July 2023 (1)
- March 2023 (1)
- February 2023 (1)
- January 2023 (1)
- December 2022 (1)
- November 2022 (1)
- September 2022 (3)
- August 2022 (1)
- June 2022 (1)
- May 2022 (2)
- April 2022 (1)
- February 2022 (3)
- January 2022 (3)
- December 2021 (1)
- November 2021 (1)
- October 2021 (2)
- September 2021 (1)
- August 2021 (13)
- July 2021 (2)
- June 2021 (1)
- April 2021 (1)
- February 2021 (1)
- January 2021 (2)
- December 2020 (1)
- July 2020 (4)
- March 2020 (4)
- January 2020 (1)
- December 2019 (1)
- November 2019 (1)
- October 2019 (1)
- August 2019 (2)
- January 2019 (1)
- December 2018 (1)
- October 2018 (2)
- September 2018 (4)
- June 2018 (1)
- August 2017 (1)
- July 2017 (1)
- May 2017 (2)
- February 2017 (1)
- January 2017 (2)
- November 2016 (1)
- September 2016 (1)
- July 2016 (1)
- June 2016 (2)
- April 2016 (4)
- March 2016 (1)
- February 2016 (1)
- January 2016 (2)
- December 2015 (2)
- August 2015 (1)
- July 2015 (1)
- May 2015 (1)
- April 2015 (2)
- March 2015 (2)
- February 2015 (2)
- January 2015 (1)
- December 2014 (1)
- October 2014 (2)
- August 2014 (1)
- July 2014 (1)
- May 2014 (2)
- February 2014 (3)
- January 2014 (1)
- July 2013 (4)
- May 2013 (2)
- March 2013 (1)
- February 2013 (1)
- January 2013 (2)
- December 2012 (1)
- November 2012 (1)
- October 2012 (1)
- September 2012 (1)
- July 2012 (2)
- May 2012 (2)
- April 2012 (2)
- March 2012 (2)
- February 2012 (1)
- January 2012 (3)
- August 2011 (3)
- July 2011 (1)
- June 2011 (2)
- May 2011 (1)
- March 2011 (2)
- February 2011 (1)
- January 2011 (4)
- December 2010 (1)
- October 2010 (1)
- August 2010 (1)
- June 2010 (1)
- May 2010 (2)
- March 2010 (1)
- February 2010 (1)
- January 2010 (2)
- December 2009 (3)
- November 2009 (3)
- October 2009 (1)
- July 2009 (2)
- May 2009 (3)
- March 2009 (2)
- February 2009 (7)
- January 2009 (10)
- November 2008 (2)
- June 2008 (1)
- April 2008 (1)
- January 2008 (1)
- December 2007 (1)
- October 2007 (1)
- June 2007 (2)
- May 2007 (1)
- April 2007 (1)
- November 2006 (2)
- October 2006 (1)
- September 2006 (2)
- June 2006 (1)
- April 2006 (2)
- January 2006 (1)
- October 2005 (1)
- July 2005 (1)
- May 2005 (2)
- April 2005 (1)
- March 2005 (1)
- December 2004 (1)
- October 2004 (1)
- November 2003 (1)
- June 2003 (1)
- May 2003 (1)
- March 2003 (2)
- December 2002 (1)
- October 2002 (1)
- July 2002 (1)
- April 2002 (2)
- March 2002 (1)
- February 2002 (2)
- October 2001 (2)
- September 2001 (1)
- August 2001 (2)
- May 2001 (1)
- March 2001 (4)
- October 2000 (3)
- July 2000 (1)
- April 2000 (1)
- March 2000 (1)
- December 1999 (1)
- August 1999 (2)
- July 1999 (1)
- June 1999 (2)
- January 1999 (2)
- October 1998 (1)
- July 1998 (1)
- June 1998 (1)
- January 1998 (1)
- November 1996 (1)
- October 1996 (1)
Post Categories
- ARCHIVES (34)
- ARTICLES (4)
- CONFERENCES (15)
- EDITORIALS (19)
- NEWS (222)
- PAST TWYPP SESSIONS (12)
- PAST WEBINARS (31)
- PATIENTS (21)
- PUBLICATIONS (1)
- RESEARCH (2)
- TALKING WITH YOUR POMPE PEEPS SESSIONS (1)
- Uncategorized (21)
- UPCOMING TWYPP SESSIONS (2)
- UPCOMING WEBINARS (2)
- WEBINARS (3)