Definition:
A form of enzyme replacement therapy used to treat Pompe disease by providing a lab-made version of the GAA enzyme.
Related Terms:
enzyme replacement therapy (ERT), avalglucosidase alfa, cipaglucosidase alfa, infusion
Apr 21, 2026
A form of enzyme replacement therapy used to treat Pompe disease by providing a lab-made version of the GAA enzyme.
enzyme replacement therapy (ERT), avalglucosidase alfa, cipaglucosidase alfa, infusion