info@amda-pompe.org

Astellas Gene Therapies Press Release – Clinical Trial Update

Jun 28, 2022 | NEWS

“On June 26, 2022, Astellas Pharma, Inc. (“Astellas”) issued a press release announcing that the U.S. Food and Drug Administration (FDA) has placed a clinical hold on the FORTIS Phase 1/2 clinical trial evaluating AT845 (“the investigational...
AMDA Zoom Webinar With Sanofi

AMDA Zoom Webinar With Sanofi

Apr 11, 2022 | PAST WEBINARS

Webinar Details Title: POMPE REGISTRY: 18 YEARS OF LEADERSHIP AND CONTRIBUTIONS Date: Monday, April 11, 2022 Speaker:Joseph Bender, MD, MBA, Global Head of Rare Disease Registries Danielle Dong, ScM, CGC, Global Operations and Advocacy Lead Rare Disease Registries...

2022 PCMA Pull for Pompe Fundraiser

Feb 28, 2022 | NEWS

The AMDA is excited to announce that the 11th Annual PCMA’s Pull for Pompe will take place on Saturday, April 30, 2022 at the National Shooting Complex in San Antonio, Texas! The Pull for Pompe clay shooting event is designed for all ages and ability levels. Please...