Dec 28, 2023 | ARCHIVES, NEWS
The AMDA is excited to announce a research grant opportunity for applicants who are involved in Pompe Disease research. This grant opportunity was made possible by the 2023 Pull for Pompe, a private fundraiser held by the Precast Manufacturer’s Association of Texas...
Nov 7, 2023 | PAST WEBINARS
Webinar Details Title: Development of Gene Therapy for Pompe Disease: Recent History Date: Tuesday, November 7, 2023 Speaker:Dr. Dwight Koeberl Webinar Overview:Dr. Koeberl will discuss the rationale for gene therapy for Pompe disease. He will provide a summary of...
Oct 17, 2023 | PAST WEBINARS
Webinar Details Title: Defining Central Nervous System Abnormalities in Infantile and Late-Onset Pompe Disease Patients Date: Tuesday, October 17, 2023 Speakers:Raquel van GoolJaymin Upadhyay Webinar Overview:In this presentation, we will provide a short description...
Oct 10, 2023 | PAST WEBINARS
Webinar Details Title: Lentiviral gene therapy for Pompe disease Date: Tuesday, October 10, 2023 Speaker:Dr. Pim Pijnappel, Associate Professor in Cell and Gene Therapy at the Erasmus MC University Medical Center, Rotterdam, the Netherlands Webinar Overview:The...
Oct 4, 2023 | ARCHIVES, NEWS
PHILADELPHIA, Sept. 28, 2023 (GLOBE NEWSWIRE) — Amicus Therapeutics (Nasdaq: FOLD) today announced that the U.S. Food and Drug Administration (FDA) has approved Pombiliti™ (cipaglucosidase alfa-atga) + Opfolda™ (miglustat) 65mg capsules. This two-component...
