Sep 25, 2018 | PAST WEBINARS
Webinar Details Title: Spark Therapeutics Gene Therapy Research Webinar Date: Tuesday, September 25, 2018 Speakers:Federico Mingozzi, PhD – Chief Scientific OfficerPaul Monahan, MD – Translation Medicine Leader, Metabolic DisordersAmy Fisher, MS, CGC...
Oct 20, 2014 | PAST WEBINARS
Webinar Details Title: Design and Performance of Clinical Trials: An Overview Date: Monday, October 20, 2014 Speaker:Anne Zajicek, MD, PharmD, FAAP, Chief, Obstetric and Pediatric, Pharmacology and Therapeutics Branch, National Institute of Child Health and Human...
Feb 27, 2014 | PAST WEBINARS
Webinar Details Title: The contribution of the IPA survey to our understanding of the natural course of Pompe disease and effects of enzyme therapy: Ten years of the IPA survey Date: Thursday, February 27, 2014 Speaker:J.C. van der Meijden, Center for Lysosomal and...
Mar 7, 2012 | PAST WEBINARS
Webinar Details Title: Needle Core Muscle Biopsy Date: Wednesday, March 7, 2012 Speaker:Mark Tarnopolsky, MD, PhD, FRCP (C) Webinar Overview:Traditionally most Neuromuscular Clinics have used an open muscle biopsy for pathological diagnosis. Many Neuromuscular...
Jan 24, 2012 | PAST WEBINARS
Webinar Details Title: NMR Imaging (MRI) and spectroscopic (NMRS) techniques for diagnosis, follow up and evaluation of Pompe disease Date: Tuesday, January 24, 2012 Speakers:Robert-Yves Carlier, MDPascal Laforêt, MDDavid Orlikowski, MD, PhDClaire Wary, PhD Webinar...
Jun 6, 2011 | PAST WEBINARS
Webinar Details Title: Respiratory Muscle Strength Training in Pompe Disease Date: Monday, June 6, 2011 Speaker:Harrison N. Jones, PhD, BRS-S, CCC-SLP, Assistant Professor, Department of Surgery, Division of Speech Pathology & Audiology, Duke University Speaker...
Feb 3, 2011 | PAST WEBINARS
Webinar Details Title: Genzyme’s Next Generation Pompe Treatment: Clinical Development Overview Date: Thursday, February 3, 2011 Speakers:Edward Kaye, MDAlison McVie-Wylie, PhD Speaker Biographies:Dr. Kaye is currently Group V.P. and Therapeutic Area Head in Clinical...
Dec 13, 2010 | PAST WEBINARS
Webinar Details Title: BMN-701: Potentially more effective treatment option for Pompe Date: Monday, December 13, 2010 Speaker: Barbara Wuebbels, BioMarinJon Lebowitz,...
Oct 26, 2010 | PAST WEBINARS
Webinar Details Title: Diaphragm Delivery of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase (rAAV1-CMV-GAA) Gene Vector in Patients With Pompe Disease Date: Tuesday, October 26, 2010 Speaker:Barry J Byrne, MD, PhD – University of...
Aug 4, 2010 | PAST WEBINARS
Webinar Details Title: Autophagy and it’s Role in Pompe Disease Date: Wednesday, August 4, 2010 Speaker:Nina Raben, MD, PhD – Staff Scientist, Arthritis + Rheumatism Branch, National Institute of Arthritis + Musculoskeletal + Skin Diseases (NIAMS), National Institutes...
