December 26, 2024
2024 AMDA/IPA International Pompe Patient and Scientific Conference Photo Gallery: May 4, 2024 Day 2 Photos Part 2
May 4, 2024: Day 2 – Conference Photos: Part 2 Previous Post: Day 2 – Conference Photos: Part 1 Next
December 26, 2024
2024 AMDA/IPA International Pompe Patient and Scientific Conference Photo Gallery: May 3, 2024 Rodeo and Dinner Part 2
May 3, 2024: Day 1 – Welcome Dinner & Rodeo: Part 2 Previous Post: Day 1 – Welcome Dinner &
December 26, 2024
2024 AMDA/IPA International Pompe Patient and Scientific Conference Photo Gallery: May 3, 2024 Rodeo and Dinner Part 1
May 3, 2024: Day 1 – Welcome Dinner & Rodeo: Part 1 After the workshops, everyone was chartered over to
December 24, 2024
2024 AMDA/IPA International Pompe Patient and Scientific Conference Photo Gallery: May 3, 2024 – Day 1 Conference
May 3, 2024 – Day 1 – Conference Photos On May 3, 2024, patients, their family members, care givers, researchers,
The AMDA is partnering with Medlive to bring this exciting program to HCPs in the Pompe community. Join leading experts
August 1, 2024
2023 Helen Walker Grant Recipient
Project title: AutophagyThe cell's internal cleanup system that removes damaged or unneeded material. More control of glycogenA stored form of sugar used for energy. More in skeletal muscleMuscles that control movement and are commonly affected in Pompe disease. More This year, the AMDA was fortunate to receive 13 grant applications focusing
We are excited to announce that the topic of our first “Talking With Your Pompe Peeps” session is “The Elementary School Experience:
University of California – San Francisco (UCSF) is excited to announce the rebranding of their phase 1 clinical trail of
February 26, 2024
Astellas Gene Therapies Webinar: Evaluating therapies for Pompe disease – clinical trial goals and assessments
Webinar Details Title: Evaluating gene therapies for Pompe diseaseA rare genetic disease in which the body cannot properly break down glycogen, leading to buildup tha... More – clinical trialA research study that tests new treatments or approaches in people. More goals and assessments Date: Monday, February 26, 2024
January 29, 2024
2024 PCMA Pull for Pompe Fundraiser
The AMDA is excited to announce that the 13th Annual PCMA’s Pull for Pompe will take place on Saturday, April
