The AMDA is partnering with Medlive to bring this exciting program to HCPs in the Pompe community. Join leading experts
August 1, 2024
2023 Helen Walker Grant Recipient
Project title: AutophagyThe cell's internal cleanup system that removes damaged or unneeded material. control of glycogenA stored form of sugar used for energy. in skeletal muscleMuscles that control movement and are commonly affected in Pompe disease. This year, the AMDA was fortunate to receive 13 grant applications focusing
We are excited to announce that the topic of our first “Talking With Your Pompe Peeps” session is “The Elementary School Experience:
University of California – San Francisco (UCSF) is excited to announce the rebranding of their phase 1 clinical trail of
February 26, 2024
Astellas Gene Therapies Webinar: Evaluating therapies for Pompe disease – clinical trial goals and assessments
Webinar Details Title: Evaluating gene therapies for Pompe diseaseA rare genetic disease in which the body cannot properly break down glycogen, leading to buildup that damages muscles and can affect breathing and, in some cases, the heart. – clinical trialA research study that tests new treatments or approaches in people. goals and assessments Date: Monday, February 26, 2024
January 29, 2024
2024 PCMA Pull for Pompe Fundraiser
The AMDA is excited to announce that the 13th Annual PCMA’s Pull for Pompe will take place on Saturday, April
The AMDA is excited to announce a research grant opportunity for applicants who are involved in Pompe Disease research. This
December 5, 2023
2024 AMDA/IPA International Conference
We are excited to announce that the 2024 AMDA/IPA International Pompe Patient and Scientific Conference will take place in San
November 7, 2023
Ask Bio Webinar: Development of Gene Therapy for Pompe Disease
Webinar Details Title: Development of Gene TherapyA developing treatment that aims to fix, replace, or add genetic instructions. for Pompe Disease: Recent History Date: Tuesday, November 7, 2023 Speaker:Dr. Dwight Koeberl
Webinar Details Title: Defining Central Nervous System Abnormalities in Infantile and Late-Onset Pompe DiseaseA form of Pompe disease that begins after infancy and usually progresses more slowly. Patients Date: Tuesday, October 17, 2023