Webinar Details Title: Development of Gene TherapyA developing treatment that aims to fix, replace, or add genetic instructions. for Pompe DiseaseA rare genetic disease in which the body cannot properly break down glycogen, leading to buildup that damages muscles and can affect breathing and, in some cases, the heart.: Recent History Date: Tuesday, November 7, 2023 Speaker:Dr. Dwight Koeberl

Webinar Details Title: Defining Central Nervous System Abnormalities in Infantile and Late-Onset Pompe DiseaseA form of Pompe disease that begins after infancy and usually progresses more slowly. Patients Date: Tuesday, October 17, 2023

Webinar Details Title: Lentiviral gene therapy for Pompe disease Date: Tuesday, October 10, 2023 Speaker:Dr. Pim Pijnappel, Associate Professor in

Webinar Details Title: Spark Therapeutics Webinar: Trail Expectations – What to Expect Date: Wednesday, September 27, 2023 Speaker:Jacose Bell Webinar

Webinar Details Title: New insights into Pompe disease since the advent of NBS Date: Thursday, August 10, 2023 Speakers:Dr. Priya