August 2, 2023
Rare Artist Contest is now Open for Submissions
Enter July 23rd – August 31st at RareArtist.org The Rare Artist Program was established in 2010 to exhibit the unique
July 7, 2023
Amicus Therapeutics Announces Approval and Launch of New Pompe Disease Therapy in the European Union
PHILADELPHIA, June 27, 2023 (GLOBE NEWSWIRE) — Amicus Therapeutics (Nasdaq: FOLD), a patient-dedicated global biotechnology company focused on developing and commercializing novel
March 28, 2023
When A Hospital and A Patient Organization Work Together & The Value of Patient Reported Outcomes
Webinar Details Title: When A Hospital and A Patient Organization Work Together & The Value of Patient Reported OutcomesInformation about health, symptoms, or quality of life reported directly by patients. Date: Tuesday,
February 8, 2023
2023 PCMA Pull for Pompe Fundraiser
The AMDA is excited to announce that the 12th Annual PCMA’s Pull for Pompe will take place on Saturday, April
The AMDA is excited to announce a research grant opportunity for applicants who are involved in Pompe DiseaseA rare genetic disease in which the body cannot properly break down glycogen, leading to buildup that damages muscles and can affect breathing and, in some cases, the heart. research. This
December 13, 2022
Insurance 101 Webinar
Webinar Details Title: Insurance 101: Learning the Basics Date: Tuesday, December 13, 2022 Speaker:Amy DeStefanis, LCSW, CCM Webinar Overview:Insurance 101
November 1, 2022
An Open Letter to the Pompe Community
On October 28, Amicus Therapeutics issued a press release with an update on the progress of our Pompe program as
September 19, 2022
International Survey on Pompe Disease and Covid-19
Over the last 2 years the COVID-19 pandemic has had wide reaching effects on people all over the world. To
September 16, 2022
In Utero ERT Webinar
Webinar Details Title: In Utero EnzymeA protein that helps the body carry out chemical reactions. Replacement Therapy for Lysosomal Storage DiseasesA group of diseases in which substances build up inside lysosomes because the body cannot break them down properly. Date: Friday, September 16, 2022 Speaker:Jeniffer L. Cohen,
September 6, 2022
2021 Helen Walker Grant for Pompe Disease Winner Announcement
The AMDA is excited to announce that the 2021 Helen Walker Grant for Pompe Disease was awarded to Dr. Peter