The AMDA is very excited to announce that the U.S. Pompe Community is one step closer to having newborn screening
The PCMA of Texas invites you to enjoy a day of family fun benefiting Acid Maltase Deficiency, also known as
February 20, 2015
Australian Pompe’s Association Welcomes Approval of Treatment for Young Australians with Pompe
Press Release by Australian Pompe Association (APA) 17th February 2015 The Australian Pompe’s Association (APA) welcomes the news that the
February 1, 2015
Second Annual International Pompe Day!
April 15th, 2015 will mark the Second Annual International Pompe Day! Last year the Pompe Community worked together to raise
January 6, 2015
Update on Biomarin’s Pompe Clinical Program—January 2015
BioMarin are pausing further recruitment for their BMN-701 clinical trial and have provided this programme update: January 2015 BioMarin is
December 15, 2014
2014 Helen Walker Research Grant Awarded
The fifth annual AMDA Research Grant (the 2014 Helen Walker Research Grant) was awarded to Dr. Giancarlo Parenti with the
October 20, 2014
Design And Performance Of Clinical Trials: An Overview
Webinar Details Title: Design and Performance of Clinical TrialsA research study that tests new treatments or approaches in people.: An Overview Date: Monday, October 20, 2014 Speaker:Anne Zajicek, MD, PharmD,
October 17, 2014
United States Pompe Community Update from Genzyme
Genzyme would like to share with you an important update regarding the recent United States (U.S.) Food and Drug Administration’s
To the United States Pompe Community: On August 1, 2014 the US Food and Drug Administration (FDA) and Genzyme issued
The AMDA is excited to announce a research grant opportunity for applicants who are involved in Pompe DiseaseA rare genetic disease in which the body cannot properly break down glycogen, leading to buildup that damages muscles and can affect breathing and, in some cases, the heart. research. This