January 6, 2015
Update on Biomarin’s Pompe Clinical Program—January 2015
BioMarin are pausing further recruitment for their BMN-701 clinical trial and have provided this programme update: January 2015 BioMarin is
December 15, 2014
2014 Helen Walker Research Grant Awarded
The fifth annual AMDA Research Grant (the 2014 Helen Walker Research Grant) was awarded to Dr. Giancarlo Parenti with the
October 20, 2014
Design And Performance Of Clinical Trials: An Overview
Webinar Details Title: Design and Performance of Clinical TrialsA research study that tests new treatments or approaches in people.: An Overview Date: Monday, October 20, 2014 Speaker:Anne Zajicek, MD, PharmD,
October 17, 2014
United States Pompe Community Update from Genzyme
Genzyme would like to share with you an important update regarding the recent United States (U.S.) Food and Drug Administration’s
To the United States Pompe Community: On August 1, 2014 the US Food and Drug Administration (FDA) and Genzyme issued
The AMDA is excited to announce a research grant opportunity for applicants who are involved in Pompe DiseaseA rare genetic disease in which the body cannot properly break down glycogen, leading to buildup that damages muscles and can affect breathing and, in some cases, the heart. research. This
May 27, 2014
BioMarin Doses First Patient in Phase 3 INSPIRE Trial with BMN 701 for the Treatment of Pompe
San Rafael, Calif., May 27, 2014 – BioMarin Pharmaceutical Inc. announced today that it has dosed the first patient with
Update: May 4, 2014 THE AMDA TO CELEBRATE THE FIRST INTERNATIONAL POMPE DAY WITH COMMEMORATIVE BOOK April 15, 2014 marked
February 27, 2014
The Contribution Of The IPA Survey To Our Understanding Of The Natural Course Of Pompe Disease
Webinar Details Title: The contribution of the IPA survey to our understanding of the natural course of Pompe disease and
February 23, 2014
2014 AMDA Pull for Pompe
On Saturday April 5, 2014 the AMDA will host the Fourth Annual Pull for Pompe at the National Shooting Complex