Jan 31, 1998 | NEWS
Human Molecular Genetics, January 1998 “Generalized glycogen storage and cardiomegaly in a knockout mouse model of Pompe disease” by A. J. J. Reuser/A. T. van der Ploeg, et al Enzyme Replacement Therapy (ERT)………. Therapy for Glycogen Storage Disease...
Nov 30, 1996 | NEWS
Johns Hopkins University Barry J. Byrne, M.D., Ph.D. Paul D. Kessler, M.D. The following is a summary of the publication in the November 1996 issue of Proceeding of the National Academy of Science, titled “Gene delivery to skeletal muscle results in sustained...
Oct 30, 1996 | NEWS
Johns Hopkin’s University scientists have successfully used a virus to supply a missing gene and its enzyme product to muscle cells in animals and humans for an extended period. The achievement could have implications in the treatment of an inherited fatal heart...
