10th Annual PCMA Pull for Pompe!

Mar 18, 2020 | NEWS

Announcement Regarding COVID-19 and the Pull for Pompe (03/18/2020): After careful consideration, and long discussions among the organizers; the 2020 PCMA Pull for Pompe has been postponed until Saturday, August 15, 2020. The Team of volunteers for The Pull For Pompe...

Upcoming Webinar: January 23, 2020

Jan 10, 2020 | NEWS

AMDA WEBINAR Title:  The common c.-32-13T>G splicing variant of GAA gene: from functional characterization to the identification of new therapeutic targets for Pompe disease. Date:  January 23, 2020 Time:  9:30am PT, 11:30am CT, 12:30pm ET Register Now: ...

2019 AMDA/IPA Conference Report Available

Dec 8, 2019 | CONFERENCES

On October 25-27, 2019, almost 200 Pompe patients and their families, scientists, doctors, and industry representatives from around the world gathered in San Antonio, Texas for the 2019 AMDA/IPA Pompe Patient and Scientific Conference.  Over the course of this...

Patient Focused Drug Development Meeting to be held March 09, 2020

Nov 22, 2019 | NEWS

The AMDA is excited to announce that it is partnering with the MDA to host a Patient Focused Drug Development Meeting (PFDD) on March 09, 2020. The PFDD meeting is an opportunity for patients and families living with Pompe disease to share their perspective and inform...