October 10, 2023
Lentiviral Gene Therapy for Pompe Disease
Webinar Details Title: Lentiviral gene therapy for Pompe disease Date: Tuesday, October 10, 2023 Speaker:Dr. Pim Pijnappel, Associate Professor in
October 4, 2023
Amicus Therapeutics Announces FDA Approval and Launch of New Treatment for Pompe Disease
PHILADELPHIA, Sept. 28, 2023 (GLOBE NEWSWIRE) — Amicus Therapeutics (Nasdaq: FOLD) today announced that the U.S. Food and Drug Administration
September 27, 2023
Spark Therapeutics Webinar: Trial Expectations
Webinar Details Title: Spark Therapeutics Webinar: Trail Expectations – What to Expect Date: Wednesday, September 27, 2023 Speaker:Jacose Bell Webinar
August 10, 2023
How to Manage LOPD Patients Diagnosed Through NBS
Webinar Details Title: New insights into Pompe disease since the advent of NBS Date: Thursday, August 10, 2023 Speakers:Dr. Priya
August 3, 2023
CALL to participate in IPA Project Every Move Counts
At International Pompe Day the International Pompe Association kicked off the Every Move Counts project. This project focuses on raising