CRANBURY, NJ, January 4, 2013 – Amicus Therapeutics today announced positive preliminary results from all 4 dose cohorts in a

AT2220 Co-Administered with EnzymeA protein that helps the body carry out chemical reactions. Replacement Therapy Second Phase 2 Pharmacological Chaperone-ERT Co-Administration Study CRANBURY, NJ, US, December 1, 2011 –

On the 30th November 2012, Helen Walker OAM (Member of the Order of Australia) passed away. Helen was a board

The path to diagnosis can be long and complicated and patients are frequently misdiagnosed along the way. In an effort

On Thursday, August 30, 2012 Dr. Arnold Reuser was decorated as a Knight in the Order of the Netherlands Lion

The AMDA is excited to announce a research grant opportunity for applicants who are involved in Pompe DiseaseA rare genetic disease in which the body cannot properly break down glycogen, leading to buildup that damages muscles and can affect breathing and, in some cases, the heart. research. This

I am very excited to announce that the 2012 PCMA’s Pull for Pompe was a HUGE success.  The PCMA of

May 13, 2012—Program Update from BioMarin. For more information about the BioMarin trials please contact Sean McCarthy of BioMarin at:

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