September 16, 2022
In Utero ERT Webinar
Webinar Details Title: In Utero Enzyme Replacement Therapy for Lysosomal Storage Diseases Date: Friday, September 16, 2022 Speaker:Jeniffer L. Cohen,
September 6, 2022
2021 Helen Walker Grant for Pompe Disease Winner Announcement
The AMDA is excited to announce that the 2021 Helen Walker Grant for Pompe Disease was awarded to Dr. Peter
August 26, 2022
Aquatic Physical Therapy Webinar
Webinar Details Title: Aquatic Exercise: Applications for Pompe Disease Date: Friday, August 26, 2022 Speaker:Dr. Kendra Lucas, PT, DPT, Aquatic
“On June 26, 2022, Astellas Pharma, Inc. (“Astellas”) issued a press release announcing that the U.S. Food and Drug Administration
The AMDA is excited to report that the final Voice of the Patient Report for the Pompe Patient-Focused Drug Development