The AMDA is writing to our Pompe patient community to let everyone know that the AMDA has been working closely

The European Medicines Agency’s (EMEA) Committee for Medicinal Products (CHMP) has recommended that infants, children and adolescents be given priority

Since the first market approval of Myozyme, the IPA has liaised directly with Genzyme LSD Therapeutics to insist that an

Since the first market approval of Myozyme, the IPA has liaised directly with Genzyme LSD Therapeutics to insist that an

This guidance is being distributed to all treating physicians worldwide except those in the European Union (EU). Separate guidance will